1.

18. The two year old child of a couple is diagnosed as having a genetic disorder ADA deficiency. They 2tried bone marrow transplantation an enzyme replacement therapy but only with a temporary cureCan you suggest a better approach of treatment for ADA defficiency?

Answer»

Types of Treatment for ADA-SCID

Three types of therapy are available for thetreatmentof ADA-SCID:

Bone marrow transplant (BMT): replaces defective immune cells with healthy immune cells from a donor

Enzyme replacement therapy (ERT): replaces the missing ADA enzyme and allows the immune system to function properly

Gene therapy:experimentaltherapy that replaces defective genes with genetically modified ones, restoring or increasing levels of ADA



Discussion

No Comment Found